Cirugía, Ciencias Médicas y Sociales
Departamento
Emory University School of Medicine
Atlanta, Estados Unidos
Publicaciones en colaboración con investigadores/as de Emory University School of Medicine (5)
2024
- Therapeutic benefit of idebenone in patients with Leber hereditary optic neuropathy: The LEROS nonrandomized controlled trial
Cell Reports Medicine, Vol. 5, Núm. 3
2023
- Indirect Comparison of Lenadogene Nolparvovec Gene Therapy Versus Natural History in Patients with Leber Hereditary Optic Neuropathy Carrying the m.11778G>A MT-ND4 Mutation
Ophthalmology and Therapy, Vol. 12, Núm. 1, pp. 401-429
- Randomized trial of bilateral gene therapy injection for m.11778G>A MT-ND4 Leber optic neuropathy
Brain : a journal of neurology, Vol. 146, Núm. 4, pp. 1328-1341
- Safety of Lenadogene Nolparvovec Gene Therapy Over 5 Years in 189 Patients With Leber Hereditary Optic Neuropathy
American Journal of Ophthalmology, Vol. 249, pp. 108-125
2022
- Study design and baseline characteristics for the reflect gene therapy trial ofm.11778g>A/ ND4-LHON
BMJ Open Ophthalmology, Vol. 7, Núm. 1
